Global Niemann-Pick Market, By Disease Type (Type A, Type B, Type C and Type E), Diagnosis (Physical Examination, Skin Biopsy, Biochemical Testing, Genetic Testing), Treatment (Miglustat, Physical Therapy and Others), Age Group (Perinatal, Early Infantile, Late Infantile, Adult) End-Users (Clinics, Hospitals, Diagnostic Centers, Others), Distribution Channel (Direct Tenders, Hospital Pharmacy, Retail Pharmacy, Online Pharmacy, Others), Country (U.S., Canada, Mexico, Brazil, Argentina, Peru, Rest of South America, Germany, France, U.K., Netherlands, Switzerland, Belgium, Russia, Italy, Spain, Turkey, Hungary, Lithuania, Austria, Ireland, Norway, Poland, Rest of Europe, China, Japan, India, South Korea, Singapore, Malaysia, Australia, Thailand, Indonesia, Philippines, Vietnam, Rest of Asia-Pacific, Saudi Arabia, U.A.E, Egypt, Israel, Kuwait, South Africa, Rest of Middle East and Africa) Industry Trends and Forecast to 2028
Market Analysis and Insights: Global Niemann-Pick Market
Niemann-Pick market is expected to gain market growth in the forecast period of 2021 to 2028. Data Bridge Market Research analyses that the market is growing at a CAGR of 5.50% in the above-mentioned research forecast period. Introduction of new tools for easy identification of Niemann-Pick disease and rising initiatives by the market players for market expansion.
Moreover growing awareness for disease symptoms and presence of pipeline drugs also boost up the market growth. Moreover technological advancements for disease diagnosis and rising healthcare expenditure act as opportunity for the market growth. But, delayed diagnosis, lack of proper screening tests and strict regulatory framework among other may hamper the global Niemann-Pick market.
Niemann-Pick is one of the rare and inherited diseases which affect the individual’s ability to metabolize cholesterol and lipids within the cells. The affected cells became malfunction and die over the time. This has been reported to affect the liver, spleen, bone marrow and lungs among others. This disease can occur at any stage of life cycle and usually affects the children. The common symptom associated with Niemann-Pick includes clumsiness, excessive muscle contraction, sleep disturbances, recurrent pneumonia among others. There are three main types of Niemann-Pick disease, type A, B and C. Niemann-Pick disease is caused due to mutation in gene responsible for production of enzyme sphingomyelinase. Niemann- Pick disease leads to several other disorders including tyrosinemia, Gaucher’s disease, and diopathic neonatal cholestasis among others.
Niemann-Pick disease can be diagnosed by the appropriate laboratory tests, skin biopsy, genetic testing, and prenatal testing among others. As it is an inherited disease prenatal testing and genetic testing are preferred more which allows the detection of defected genes responsible for disease symptoms.
Patients suffering from Niemann-Pick disease are usually prescribed with miglustat (Zavesca) drug which has been reported to improve the neurological symptoms associated with the disease. Moreover, physical therapy also proved advantageous for the treatment of Niemann-Pick disease.
The prevalence of inherited genes is increasing worldwide which including Niemann-Pick among others, moreover growing infants populations are at high risk of developing inherited disease and hence expected to provide market with the lucrative growth. It is also estimated that Niemann-Pick market is growing with the CAGR of 6.40% in 2020.
This Niemann-Pick market provides details of market share, new developments and product pipeline analysis, impact of domestic and localized market players, analyses opportunities in terms of emerging revenue pockets, changes in market regulations, product approvals, strategic decisions, product launches, geographic expansions and technological innovations in the market. To understand the analysis and the market scenario contact us for an Analyst Brief, our team will help you create a revenue impact solution to achieve your desired goal.
Global Niemann-Pick Market Scope and Market Size
Niemann-Pick market is segmented on the basis of disease type, diagnosis, treatment, end-users and distribution channel. The growth among segments helps you analyse niche pockets of growth and strategies to approach the market and determine your core application areas and the difference in your target markets.
- On the basis of disease type, the Niemann-Pick market is segmented into Type A, Type B, Type C and Type E.
- On the basis of diagnosis, the Niemann-Pick market is segmented into physical examination, skin biopsy, biochemical testing, and genetic testing.
- On the basis of treatment, the Niemann-Pick market is segmented into miglustat, physical therapy and others.
- On the basis of end-users, the Niemann-Pick market is segmented into clinics, hospitals, diagnostic centers, and others.
- On the basis of distribution channel, the Niemann-Pick market is segmented into direct tenders, hospital pharmacy, retail pharmacy, online pharmacy and others.
Niemann-Pick Market Country Level Analysis
Niemann-Pick market is analysed and market size information is provided by country, type, diagnosis, treatment, end-users and distribution channel as referenced above.
The countries covered in the Niemann-Pick market report are U.S., Canada, Mexico in North America, Brazil, Argentina, Peru, Rest of South America, as part of South America, Germany, France, U.K., Netherlands, Switzerland, Belgium, Russia, Italy, Spain, Turkey, Hungary, Lithuania, Austria, Ireland, Norway, Poland, Rest of Europe in Europe, China, Japan, India, South Korea, Singapore, Malaysia, Australia, Thailand, Indonesia, Philippines, Vietnam, Rest of Asia-Pacific, Saudi Arabia, U.A.E, Egypt, Israel, Kuwait, South Africa, Rest of Middle East and Africa, as a part of Middle East and Africa.
On geographical estimation, North America accounts the largest market share due to the increasing research and developmental activities and rising technological advancements. Europe is also expected to grow exponentially due to rising cases of people affected with Niemann- Pick disease that demonstrates approximately 0.1 in every 10,000 people. Moreover orphan drug designation provided to the miglustat by European Union also accelerates the market growth. Asia-Pacific is expected to account for the largest market share owing to increasing prevalence of inherited disorders and increasing government concern for newborns health.
The country section of the report also provides individual market impacting factors and changes in regulations in the market domestically that impacts the current and future trends of the market. Data points such as new sales, replacement sales, country demographics, disease epidemiology and import-export tariffs are some of the major pointers used to forecast the market scenario for individual countries. Also, presence and availability of global brands and their challenges faced due to large or scarce competition from local and domestic brands, impact of sales channels are considered while providing forecast analysis of the country data.
Patient Epidemiology Analysis
Niemann-Pick market also provides you with detailed market analysis for patient analysis, prognosis and cures. Prevalence, incidence, mortality, adherence rates are some of the data variables that are available in the report. Direct or indirect impact analysis of epidemiology to market growth are analysed to create a more robust and cohort multivariate statistical model for forecasting the market in the growth period.
Competitive Landscape and Niemann-Pick Market Share Analysis
Niemann-Pick market competitive landscape provides details by competitor details included are company overview, company financials, revenue generated, market potential, investment in research and development, new market initiatives, global presence, production sites and facilities, company strengths and weaknesses, product launch, clinical trials pipelines, product approvals, patents, product width and breadth, application dominance, technology lifeline curve. The above data points provided are only related to the companies’ focus related to Niemann-Pick market.
The major players covered in the Niemann-Pick market are Orphazyme ApS, CTD Holdings Inc, Neurotrope Inc, Okklo Life Sciences, Intrabio, Azafaros, CENTOGENE N.V., Actelion Pharmaceuticals Ltd, Mallinckrodt, Merck & Co., Inc., Alexion Pharmaceuticals, Genzyme Corporation, Cyclo Therapeutics, Inc., DIPHARMA SA, Apothecon Pharmaceuticals Pvt. Ltd. and Aldagen Inc., evox Therapeutics, among other domestic and global players. DBMR analysts understand competitive strengths and provide competitive analysis for each competitor separately.
SKU-